1.
Over the last few decades, the utility of viral vectors has expanded from their initial use as clinical therapeutics for debilitating genetic diseases to include their us [...]
2020 | Dissertation |
2.
The main focus of this dissertation work was to advance gene therapy research for phenylketonuria (PKU). PKU is an inborn error of metabolism characterized by phenylalani [...]
2020 | Dissertation |
3.
This dissertation describes the development of the TRADE system for directed evolution of the AAV capsid, its successful application to identify the HN1 variant, a novel [...]
2021 | Dissertation |