1.
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Over the last few decades, the utility of viral vectors has expanded from their initial use as clinical therapeutics for debilitating genetic diseases to include their us [...]
2020 |
Dissertation |
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2.
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The main focus of this dissertation work was to advance gene therapy research for phenylketonuria (PKU). PKU is an inborn error of metabolism characterized by phenylalani [...]
2020 |
Dissertation |
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3.
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This dissertation describes the development of the TRADE system for directed evolution of the AAV capsid, its successful application to identify the HN1 variant, a novel [...]
2021 |
Dissertation |
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