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1.
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The main focus of this dissertation work was to advance gene therapy research for phenylketonuria (PKU). PKU is an inborn error of metabolism characterized by phenylalani [...]
2020 |
Dissertation |
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2.
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1990s?
1990 |
Still image |
Historical Collections and Archives |
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3.
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The goal of this dissertation is to improve understanding and treatment for the chorioretinopathy seen in long-chain 3-hydroxyacyl-CoA dehydrogenase deficiency (LCHADD) p [...]
2024-06-13 |
Dissertation |
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4.
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This dissertation describes the development of the TRADE system for directed evolution of the AAV capsid, its successful application to identify the HN1 variant, a novel [...]
2021 |
Dissertation |
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5.
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Diabetes mellitus is a group of metabolic disorders characterized by prolonged elevation of
blood glucose levels, inducing numerous complications such [...]
2017 |
Thesis |
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6.
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Liver-directed gene and cell therapies represent a promising therapeutic strategy for many genetic disorders. However, they are hampered by inefficiency. The problem of i [...]
2023-12-15 |
Dissertation |
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7.
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8.
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